To treat large gaps in long bones, like the femur, which result from bone tumor removal or a shattering trauma,
Category: Gene therapy
Newly Approved Spinal Muscle Atrophy Treatment Zolgensma is Based on Delivery System Discovered by Penn Gene Therapy Pioneer
James Wilson, MD, PhD, recalls being struck by the devastating toll of rare diseases as a young physician in the 1980s.
Gene Therapy Shows Initial Promise for Parkinson’s Disease
A delicate operation that involved placing a gene into the brain was found to reduce the severity of motor symptoms
Initiative Will Create Coursework for Cell Manufacturing Workers
An 18-month federally-sponsored project led by the Georgia Institute of Technology will develop much-needed curriculum to train workers for the
Gene therapy for type 1 diabetes
Type 1 diabetes is a chronic disease in which the immune system attacks and destroys insulin-producing beta cells in the
Gene therapy may kill HIV
Gene therapy may have the potential to eradicate HIV in people infected with the virus, new animal research suggests. The
Gene therapy can destroy HIV infected cells
Through gene therapy, researchers engineered blood-forming stem cells (hematopoietic stem/progenitor cells, or HSPCs) to carry chimeric antigen receptor (CAR) genes
Luxturna for treating inherited retinal disease
Luxturna (voretigene neparvovec) is an adeno-associated viral (AAV) vector gene therapy for the treatment of patients with vision loss due
